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Multidimensional Response Surface Methodology for the Development of a Gene Editing Protocol for p67phox-Deficient Chronic Granulomatous Disease.
Whittaker, Thomas E; Moula, Shefta E; Bahal, Sameer; Bakri, Faris Ghalib; Hayajneh, Wail Ahmad; Daoud, Ammar Khaled; Naseem, Asma; Cavazza, Alessia; Thrasher, Adrian J; Santilli, Giorgia.
Afiliación
  • Whittaker TE; Infection, Immunity, and Inflammation Research and Teaching Department, UCL, Great Ormond Street Institute of Child Health, University College London, London, United Kingdom.
  • Moula SE; Infection, Immunity, and Inflammation Research and Teaching Department, UCL, Great Ormond Street Institute of Child Health, University College London, London, United Kingdom.
  • Bahal S; Infection, Immunity, and Inflammation Research and Teaching Department, UCL, Great Ormond Street Institute of Child Health, University College London, London, United Kingdom.
  • Bakri FG; Division of Infectious Diseases, Department of Medicine, Jordan University Hospital, Amman, Jordan.
  • Hayajneh WA; Infectious Diseases and Vaccine Center, University of Jordan, Amman, Jordan.
  • Daoud AK; Division of Infectious Diseases, Department of Pediatrics, Jordan University of Science & Technology, Irbid, Jordan.
  • Naseem A; Division of Immunology, Department of Internal Medicine, Jordan University of Science & Technology, Irbid, Jordan.
  • Cavazza A; Infection, Immunity, and Inflammation Research and Teaching Department, UCL, Great Ormond Street Institute of Child Health, University College London, London, United Kingdom.
  • Thrasher AJ; Infection, Immunity, and Inflammation Research and Teaching Department, UCL, Great Ormond Street Institute of Child Health, University College London, London, United Kingdom.
  • Santilli G; Infection, Immunity, and Inflammation Research and Teaching Department, UCL, Great Ormond Street Institute of Child Health, University College London, London, United Kingdom.
Hum Gene Ther ; 35(7-8): 298-312, 2024 Apr.
Article en En | MEDLINE | ID: mdl-38062734

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedad Granulomatosa Crónica Límite: Humans Idioma: En Revista: Hum Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2024 Tipo del documento: Article País de afiliación: Reino Unido Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedad Granulomatosa Crónica Límite: Humans Idioma: En Revista: Hum Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2024 Tipo del documento: Article País de afiliación: Reino Unido Pais de publicación: Estados Unidos