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Thrombotic microangiopathy following systemic AAV administration is dependent on anti-capsid antibodies.
Salabarria, Stephanie M; Corti, Manuela; Coleman, Kirsten E; Wichman, Megan B; Berthy, Julie A; D'Souza, Precilla; Tifft, Cynthia J; Herzog, Roland W; Elder, Melissa E; Shoemaker, Lawrence R; Leon-Astudillo, Carmen; Tavakkoli, Fatemeh; Kirn, David H; Schwartz, Jonathan D; Byrne, Barry J.
Afiliación
  • Salabarria SM; Department of Pediatrics, University of Florida, Gainesville, Florida, USA.
  • Corti M; Department of Pediatrics, University of Florida, Gainesville, Florida, USA.
  • Coleman KE; Department of Pediatrics, University of Florida, Gainesville, Florida, USA.
  • Wichman MB; Department of Pediatrics, University of Florida, Gainesville, Florida, USA.
  • Berthy JA; Department of Pediatrics, University of Florida, Gainesville, Florida, USA.
  • D'Souza P; National Human Genome Research Institute, NIH, Bethesda, Maryland, USA.
  • Tifft CJ; National Human Genome Research Institute, NIH, Bethesda, Maryland, USA.
  • Herzog RW; Indiana University, South Bend, Indiana, USA.
  • Elder ME; Department of Pediatrics, University of Florida, Gainesville, Florida, USA.
  • Shoemaker LR; Department of Pediatrics, University of Florida, Gainesville, Florida, USA.
  • Leon-Astudillo C; Department of Pediatrics, University of Florida, Gainesville, Florida, USA.
  • Tavakkoli F; 4D Molecular Therapeutics, Emeryville, California, USA.
  • Kirn DH; 4D Molecular Therapeutics, Emeryville, California, USA.
  • Schwartz JD; Rocket Pharma, Cranbury, New Jersey, USA.
  • Byrne BJ; Department of Pediatrics, University of Florida, Gainesville, Florida, USA.
J Clin Invest ; 134(1)2024 Jan 02.
Article en En | MEDLINE | ID: mdl-37988172

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Dependovirus / Microangiopatías Trombóticas Límite: Humans Idioma: En Revista: J Clin Invest Año: 2024 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Dependovirus / Microangiopatías Trombóticas Límite: Humans Idioma: En Revista: J Clin Invest Año: 2024 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Estados Unidos