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Study methodology and insights from the palovarotene clinical development program in fibrodysplasia ossificans progressiva.
Pignolo, Robert J; Al Mukaddam, Mona; Baujat, Geneviève; Brown, Matthew A; De Cunto, Carmen; Hsiao, Edward C; Keen, Richard; Le Quan Sang, Kim-Hanh; Grogan, Donna R; Marino, Rose; Strahs, Andrew R; Kaplan, Frederick S.
Afiliación
  • Pignolo RJ; Department of Medicine, Mayo Clinic, Rochester, MN, US.
  • Al Mukaddam M; Departments of Orthopedic Surgery & Medicine, The Center for Research in FOP and Related Disorders, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, US.
  • Baujat G; Département de Génétique, Institut Imagine, Hôpital Universitaire Necker-Enfants Malades, Université Paris Cité, Paris, France.
  • Brown MA; Faculty of Life Sciences and Medicine, King's College London, and Genomics England Ltd, London, UK.
  • De Cunto C; Pediatric Rheumatology Section, Department of Pediatrics, Hospital Italiano de Buenos Aires, Buenos Aires, Argentina.
  • Hsiao EC; Division of Endocrinology and Metabolism, the UCSF Metabolic Bone Clinic, the Eli and Edythe Broad Institute for Regeneration Medicine, and the Institute of Human Genetics, Department of Medicine, and the UCSF Program in Craniofacial Biology, University of California-San Francisco, San Francisco, CA
  • Keen R; Centre for Metabolic Bone Disease, Royal National Orthopaedic Hospital, Stanmore, UK.
  • Le Quan Sang KH; Département de Génétique, Institut Imagine, Hôpital Universitaire Necker-Enfants Malades, Université Paris Cité, Paris, France.
  • Grogan DR; Ipsen, Cambridge, MA, US.
  • Marino R; Ipsen, Cambridge, MA, US. rosemarino@yahoo.com.
  • Strahs AR; Ipsen, Cambridge, MA, US.
  • Kaplan FS; Departments of Orthopedic Surgery & Medicine, The Center for Research in FOP and Related Disorders, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, US.
BMC Med Res Methodol ; 23(1): 269, 2023 11 13.
Article en En | MEDLINE | ID: mdl-37957586

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Osificación Heterotópica / Miositis Osificante Límite: Humans Idioma: En Revista: BMC Med Res Methodol Asunto de la revista: MEDICINA Año: 2023 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Osificación Heterotópica / Miositis Osificante Límite: Humans Idioma: En Revista: BMC Med Res Methodol Asunto de la revista: MEDICINA Año: 2023 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Reino Unido