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Impact of nusinersen on the health-related quality of life and caregiver burden of patients with spinal muscular atrophy with symptom onset after age 6 months.
Lee, Yun Jeong; Kim, Ae Ryoung; Lee, Jong-Mok; Shim, Young Kyu; Cho, Jae So; Ryu, Hye Won; Kwon, Soonhak; Chae, Jong-Hee.
Afiliación
  • Lee YJ; Department of Pediatrics, Kyungpook National University Hospital and School of Medicine, Kyungpook National University, Daegu, South Korea.
  • Kim AR; Department of Rehabilitation Medicine, Kyungpook National University Hospital and School of Medicine, Kyungpook National University, Daegu, South Korea.
  • Lee JM; Department of Neurology, Kyungpook National University Hospital and School of Medicine, Kyungpook National University, Daegu, South Korea.
  • Shim YK; Department of Pediatrics, Korea University Ansan Hospital, Seoul, South Korea.
  • Cho JS; Department of Pediatrics, Pediatric Clinical Neuroscience Center, Seoul National University Children's Hospital, Seoul National University College of Medicine, Seoul, South Korea.
  • Ryu HW; Department of Pediatrics, Pediatric Clinical Neuroscience Center, Seoul National University Children's Hospital, Seoul National University College of Medicine, Seoul, South Korea.
  • Kwon S; Department of Pediatrics, Kyungpook National University Children's Hospital, School of Medicine, Kyungpook National University, Daegu, South Korea.
  • Chae JH; Department of Pediatrics, Pediatric Clinical Neuroscience Center, Seoul National University Children's Hospital, Seoul National University College of Medicine, Seoul, South Korea.
Muscle Nerve ; 68(4): 404-413, 2023 10.
Article en En | MEDLINE | ID: mdl-37602664

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Atrofia Muscular Espinal / Carga del Cuidador Tipo de estudio: Diagnostic_studies / Prognostic_studies Aspecto: Patient_preference Límite: Child / Humans / Infant Idioma: En Revista: Muscle Nerve Año: 2023 Tipo del documento: Article País de afiliación: Corea del Sur Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Atrofia Muscular Espinal / Carga del Cuidador Tipo de estudio: Diagnostic_studies / Prognostic_studies Aspecto: Patient_preference Límite: Child / Humans / Infant Idioma: En Revista: Muscle Nerve Año: 2023 Tipo del documento: Article País de afiliación: Corea del Sur Pais de publicación: Estados Unidos