Your browser doesn't support javascript.
loading
Engineered tRNAs suppress nonsense mutations in cells and in vivo.
Albers, Suki; Allen, Elizabeth C; Bharti, Nikhil; Davyt, Marcos; Joshi, Disha; Perez-Garcia, Carlos G; Santos, Leonardo; Mukthavaram, Rajesh; Delgado-Toscano, Miguel Angel; Molina, Brandon; Kuakini, Kristen; Alayyoubi, Maher; Park, Kyoung-Joo Jenny; Acharya, Grishma; Gonzalez, Jose A; Sagi, Amit; Birket, Susan E; Tearney, Guillermo J; Rowe, Steven M; Manfredi, Candela; Hong, Jeong S; Tachikawa, Kiyoshi; Karmali, Priya; Matsuda, Daiki; Sorscher, Eric J; Chivukula, Pad; Ignatova, Zoya.
Afiliación
  • Albers S; Institute of Biochemistry and Molecular Biology, University of Hamburg, Hamburg, Germany.
  • Allen EC; Arcturus Therapeutics, San Diego, CA, USA.
  • Bharti N; Institute of Biochemistry and Molecular Biology, University of Hamburg, Hamburg, Germany.
  • Davyt M; Institute of Biochemistry and Molecular Biology, University of Hamburg, Hamburg, Germany.
  • Joshi D; Department of Pediatrics, School of Medicine, Emory University, Atlanta, GA, USA.
  • Perez-Garcia CG; Children's Healthcare of Atlanta, Atlanta, GA, USA.
  • Santos L; Arcturus Therapeutics, San Diego, CA, USA.
  • Mukthavaram R; Institute of Biochemistry and Molecular Biology, University of Hamburg, Hamburg, Germany.
  • Delgado-Toscano MA; Arcturus Therapeutics, San Diego, CA, USA.
  • Molina B; Institute of Biochemistry and Molecular Biology, University of Hamburg, Hamburg, Germany.
  • Kuakini K; Arcturus Therapeutics, San Diego, CA, USA.
  • Alayyoubi M; Arcturus Therapeutics, San Diego, CA, USA.
  • Park KJ; Arcturus Therapeutics, San Diego, CA, USA.
  • Acharya G; Arcturus Therapeutics, San Diego, CA, USA.
  • Gonzalez JA; Arcturus Therapeutics, San Diego, CA, USA.
  • Sagi A; Arcturus Therapeutics, San Diego, CA, USA.
  • Birket SE; Arcturus Therapeutics, San Diego, CA, USA.
  • Tearney GJ; Pulmonary, Allergy, and Critical Care Medicine, University of Alabama at Birmingham, Birmingham, AL, USA.
  • Rowe SM; Wellman Center for Photomedicine, Massachusetts General Hospital, Boston, MA, USA.
  • Manfredi C; Harvard-MIT Health Sciences and Technology, MA, Cambridge, USA.
  • Hong JS; Pulmonary, Allergy, and Critical Care Medicine, University of Alabama at Birmingham, Birmingham, AL, USA.
  • Tachikawa K; Department of Pediatrics, School of Medicine, Emory University, Atlanta, GA, USA.
  • Karmali P; Children's Healthcare of Atlanta, Atlanta, GA, USA.
  • Matsuda D; Department of Pediatrics, School of Medicine, Emory University, Atlanta, GA, USA.
  • Sorscher EJ; Children's Healthcare of Atlanta, Atlanta, GA, USA.
  • Chivukula P; Arcturus Therapeutics, San Diego, CA, USA.
  • Ignatova Z; Arcturus Therapeutics, San Diego, CA, USA.
Nature ; 618(7966): 842-848, 2023 Jun.
Article en En | MEDLINE | ID: mdl-37258671

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: ARN de Transferencia / Codón sin Sentido / Regulador de Conductancia de Transmembrana de Fibrosis Quística Límite: Animals Idioma: En Revista: Nature Año: 2023 Tipo del documento: Article País de afiliación: Alemania Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: ARN de Transferencia / Codón sin Sentido / Regulador de Conductancia de Transmembrana de Fibrosis Quística Límite: Animals Idioma: En Revista: Nature Año: 2023 Tipo del documento: Article País de afiliación: Alemania Pais de publicación: Reino Unido