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Efficacy and Safety of Leriglitazone in Patients With Friedreich Ataxia: A Phase 2 Double-Blind, Randomized Controlled Trial (FRAMES).
Pandolfo, Massimo; Reetz, Kathrin; Darling, Alejandra; Rodriguez de Rivera, Francisco Javier; Henry, Pierre-Gilles; Joers, James; Lenglet, Christophe; Adanyeguh, Isaac; Deelchand, Dinesh; Mochel, Fanny; Pousset, Françoise; Pascual, Sílvia; Van den Eede, Delphine; Martin-Ugarte, Itziar; Vilà-Brau, Anna; Mantilla, Adriana; Pascual, María; Martinell, Marc; Meya, Uwe; Durr, Alexandra.
Afiliación
  • Pandolfo M; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Reetz K; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Darling A; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Rodriguez de Rivera FJ; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Henry PG; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Joers J; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Lenglet C; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Adanyeguh I; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Deelchand D; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Mochel F; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Pousset F; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Pascual S; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Van den Eede D; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Martin-Ugarte I; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Vilà-Brau A; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Mantilla A; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Pascual M; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Martinell M; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Meya U; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
  • Durr A; Université Libre de Bruxelles (M. Pandolfo), Brussels, Belgium; Department of Neurology (K.R.), RWTH Aachen University, Germany; JARA-BRAIN Institute Molecular Neuroscience and Neuroimaging (K.R.), Forschungszentrum Jülich GmbH, Germany; Hospital Sant Joan de Déu (A. Darling), Barcelona, Spain; La P
Neurol Genet ; 8(6): e200034, 2022 Dec.
Article en En | MEDLINE | ID: mdl-36524101

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Tipo de estudio: Clinical_trials / Prognostic_studies Idioma: En Revista: Neurol Genet Año: 2022 Tipo del documento: Article Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Tipo de estudio: Clinical_trials / Prognostic_studies Idioma: En Revista: Neurol Genet Año: 2022 Tipo del documento: Article Pais de publicación: Estados Unidos