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Liver-directed drugs for transthyretin-mediated amyloidosis.
Brannagan, Thomas H; Berk, John L; Gillmore, Julian D; Maurer, Mathew S; Waddington-Cruz, Márcia; Fontana, Marianna; Masri, Ahmad; Obici, Laura; Brambatti, Michela; Baker, Brenda F; Hannan, Lisa A; Buchele, Gustavo; Viney, Nick J; Coelho, Teresa; Nativi-Nicolau, Jose.
Afiliación
  • Brannagan TH; Peripheral Neuropathy Center, Columbia University, Vagelos College of Physicians and Surgeons, New York, New York, USA.
  • Berk JL; Amyloidosis Center, Boston University School of Medicine, Boston, Massachusetts, USA.
  • Gillmore JD; National Amyloidosis Centre, University College London, Royal Free Hospital, London, UK.
  • Maurer MS; Cardiac Amyloidosis Program, Division of Cardiology, Columbia College of Physicians and Surgeons, New York, New York, USA.
  • Waddington-Cruz M; National Amyloidosis Referral Center-CEPARM, University Hospital, Federal University of Rio de Janeiro, Rio de Janeiro, Brazil.
  • Fontana M; National Amyloidosis Centre, University College London, Royal Free Hospital, London, UK.
  • Masri A; Cardiac Amyloidosis Program, Knight Cardiovascular Institute, Oregon Health & Science University, Portland, Oregon, USA.
  • Obici L; Amyloidosis Research and Treatment Center, IRCCS Fondazione Policlinico San Matteo, Pavia, Italy.
  • Brambatti M; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.
  • Baker BF; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.
  • Hannan LA; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.
  • Buchele G; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.
  • Viney NJ; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.
  • Coelho T; Department of Neurosciences, Centro Hospitalar Universitário do Porto, Porto, Portugal.
  • Nativi-Nicolau J; Division of Heart Failure and Transplant, Mayo Clinic, Jacksonville, Florida, USA.
J Peripher Nerv Syst ; 27(4): 228-237, 2022 12.
Article en En | MEDLINE | ID: mdl-36345805

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Prealbúmina / Neuropatías Amiloides Familiares Límite: Humans Idioma: En Revista: J Peripher Nerv Syst Asunto de la revista: NEUROLOGIA Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Prealbúmina / Neuropatías Amiloides Familiares Límite: Humans Idioma: En Revista: J Peripher Nerv Syst Asunto de la revista: NEUROLOGIA Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Estados Unidos