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Long-term bone outcomes in Italian patients with Gaucher disease type 1 or type 3 treated with imiglucerase: A sub-study from the International Collaborative Gaucher Group (ICGG) Gaucher Registry.
Cappellini, Maria Domenica; Carubbi, Francesca; Di Rocco, Maja; Giona, Fiorina; Giuffrida, Gaetano.
Afiliación
  • Cappellini MD; Department of Clinical Sciences and Community, Fondazione Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) Ca' Granda Policlinico Hospital, University of Milan, Milan, Italy. Electronic address: maria.cappellini@unimi.it.
  • Carubbi F; Unit of Internal Metabolic Medicine, University Hospital of Modena and Department of Biomedical, Metabolic and Neural Sciences, University of Modena and Reggio Emilia, Modena, Italy. Electronic address: francesca.carubbi@unimore.it.
  • Di Rocco M; IRCCS Istituto Giannina Gaslini, Via Gaslini 5, Genova, Italy. Electronic address: majadirocco@gaslini.org.
  • Giona F; Hematology, Department of Translational and Precision Medicine, Sapienza University of Roma, AOU Policlinico Umberto I, Rome, Italy. Electronic address: giona@bce.uniroma1.it.
  • Giuffrida G; Division of Hematology, AOU "Policlinico G. Rodolico-San Marco", Catania, Italy.
Blood Cells Mol Dis ; 98: 102705, 2023 01.
Article en En | MEDLINE | ID: mdl-36327675

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedades Óseas / Enfermedad de Gaucher Límite: Humans Idioma: En Revista: Blood Cells Mol Dis Asunto de la revista: HEMATOLOGIA Año: 2023 Tipo del documento: Article Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedades Óseas / Enfermedad de Gaucher Límite: Humans Idioma: En Revista: Blood Cells Mol Dis Asunto de la revista: HEMATOLOGIA Año: 2023 Tipo del documento: Article Pais de publicación: Estados Unidos