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A phase II, multicenter, open-label trial to evaluate the safety and efficacy of ISU303 (Agalsidase beta) in patients with Fabry disease.
Hwang, Soojin; Lee, Beom Hee; Kim, Woo-Shik; Kim, Dae-Seong; Cheon, Chong Kun; Lee, Chang Hwa; Choi, Yunha; Choi, Jin-Ho; Kim, Ja Hye; Yoo, Han-Wook.
Afiliación
  • Hwang S; Department of Pediatrics, Asan Medical Center Children's Hospital, University of Ulsan College of Medicine, Seoul, Korea.
  • Lee BH; Department of Pediatrics, Asan Medical Center Children's Hospital, University of Ulsan College of Medicine, Seoul, Korea.
  • Kim WS; Medical Genetics Center, Asan Medical Center Children's Hospital, University of Ulsan College of Medicine, Seoul, Korea.
  • Kim DS; Department of Internal Medicine, Kyung Hee University College of Medicine, Seoul, Korea.
  • Cheon CK; Department of Neurology, Pusan National University Yangsan Hospital, Pusan National University School of Medicine, Yangsan, Korea.
  • Lee CH; Department of Pediatrics, Pusan National University Yangsan Hospital, Pusan National University School of Medicine, Yangsan, Korea.
  • Choi Y; Department of Internal Medicine, Hanyang University Medical Center, Seoul, Korea.
  • Choi JH; Department of Pediatrics, Asan Medical Center Children's Hospital, University of Ulsan College of Medicine, Seoul, Korea.
  • Kim JH; Department of Pediatrics, Asan Medical Center Children's Hospital, University of Ulsan College of Medicine, Seoul, Korea.
  • Yoo HW; Department of Pediatrics, Asan Medical Center Children's Hospital, University of Ulsan College of Medicine, Seoul, Korea.
Medicine (Baltimore) ; 101(37): e30345, 2022 Sep 16.
Article en En | MEDLINE | ID: mdl-36123934

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedad de Fabry / Alfa-Galactosidasa Tipo de estudio: Clinical_trials / Diagnostic_studies Aspecto: Patient_preference Límite: Female / Humans / Male Idioma: En Revista: Medicine (Baltimore) Año: 2022 Tipo del documento: Article Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedad de Fabry / Alfa-Galactosidasa Tipo de estudio: Clinical_trials / Diagnostic_studies Aspecto: Patient_preference Límite: Female / Humans / Male Idioma: En Revista: Medicine (Baltimore) Año: 2022 Tipo del documento: Article Pais de publicación: Estados Unidos