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Allele-Selective LNA Gapmers for the Treatment of Fibrodysplasia Ossificans Progressiva Knock Down the Pathogenic ACVR1R206H Transcript and Inhibit Osteogenic Differentiation.
Maruyama, Rika; Nguyen, Quynh; Roshmi, Rohini Roy; Touznik, Aleksander; Yokota, Toshifumi.
Afiliación
  • Maruyama R; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, Canada.
  • Nguyen Q; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, Canada.
  • Roshmi RR; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, Canada.
  • Touznik A; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, Canada.
  • Yokota T; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, Canada.
Nucleic Acid Ther ; 32(3): 185-193, 2022 06.
Article en En | MEDLINE | ID: mdl-35085461

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Osificación Heterotópica / Miositis Osificante Límite: Humans Idioma: En Revista: Nucleic Acid Ther Año: 2022 Tipo del documento: Article País de afiliación: Canadá Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Osificación Heterotópica / Miositis Osificante Límite: Humans Idioma: En Revista: Nucleic Acid Ther Año: 2022 Tipo del documento: Article País de afiliación: Canadá Pais de publicación: Estados Unidos