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Correction of a Factor VIII genomic inversion with designer-recombinases.
Lansing, Felix; Mukhametzyanova, Liliya; Rojo-Romanos, Teresa; Iwasawa, Kentaro; Kimura, Masaki; Paszkowski-Rogacz, Maciej; Karpinski, Janet; Grass, Tobias; Sonntag, Jan; Schneider, Paul Martin; Günes, Ceren; Hoersten, Jenna; Schmitt, Lukas Theo; Rodriguez-Muela, Natalia; Knöfler, Ralf; Takebe, Takanori; Buchholz, Frank.
Afiliación
  • Lansing F; Medical Systems Biology, Medical Faculty, Technical University Dresden, 01307, Dresden, Germany.
  • Mukhametzyanova L; Medical Systems Biology, Medical Faculty, Technical University Dresden, 01307, Dresden, Germany.
  • Rojo-Romanos T; Medical Systems Biology, Medical Faculty, Technical University Dresden, 01307, Dresden, Germany.
  • Iwasawa K; Division of Gastroenterology, Hepatology and Nutrition, Division of Developmental Biology, Center for Stem Cell and Organoid Medicine (CuSTOM) Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Kimura M; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH, USA.
  • Paszkowski-Rogacz M; Division of Gastroenterology, Hepatology and Nutrition, Division of Developmental Biology, Center for Stem Cell and Organoid Medicine (CuSTOM) Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Karpinski J; Medical Systems Biology, Medical Faculty, Technical University Dresden, 01307, Dresden, Germany.
  • Grass T; Medical Systems Biology, Medical Faculty, Technical University Dresden, 01307, Dresden, Germany.
  • Sonntag J; Medical Systems Biology, Medical Faculty, Technical University Dresden, 01307, Dresden, Germany.
  • Schneider PM; German Center for Neurodegenerative Diseases, Helmholtz Association, 01307, Dresden, Germany.
  • Günes C; Medical Systems Biology, Medical Faculty, Technical University Dresden, 01307, Dresden, Germany.
  • Hoersten J; Medical Systems Biology, Medical Faculty, Technical University Dresden, 01307, Dresden, Germany.
  • Schmitt LT; Department of Cell and Developmental Biology, Max Planck Institute for Molecular Biomedicine, Röntgenstrasse 20, Münster, 48149, Germany.
  • Rodriguez-Muela N; Medical Systems Biology, Medical Faculty, Technical University Dresden, 01307, Dresden, Germany.
  • Knöfler R; Medical Systems Biology, Medical Faculty, Technical University Dresden, 01307, Dresden, Germany.
  • Takebe T; German Center for Neurodegenerative Diseases, Helmholtz Association, 01307, Dresden, Germany.
  • Buchholz F; Department of Pediatric Hematology and Oncology, University Hospital Dresden, 01307, Dresden, Germany.
Nat Commun ; 13(1): 422, 2022 01 20.
Article en En | MEDLINE | ID: mdl-35058465

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Factor VIII / Recombinasas / Inversión Cromosómica Límite: Humans Idioma: En Revista: Nat Commun Asunto de la revista: BIOLOGIA / CIENCIA Año: 2022 Tipo del documento: Article País de afiliación: Alemania Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Factor VIII / Recombinasas / Inversión Cromosómica Límite: Humans Idioma: En Revista: Nat Commun Asunto de la revista: BIOLOGIA / CIENCIA Año: 2022 Tipo del documento: Article País de afiliación: Alemania Pais de publicación: Reino Unido