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Safe and Effective Cynomolgus Monkey GLP-Tox Study with Repetitive Intrathecal Application of a TGFBR2 Targeting LNA-Gapmer Antisense Oligonucleotide as Treatment Candidate for Neurodegenerative Disorders.
Peters, Sebastian; Wirkert, Eva; Kuespert, Sabrina; Heydn, Rosmarie; Johannesen, Siw; Friedrich, Anita; Mailänder, Susanne; Korte, Sven; Mecklenburg, Lars; Aigner, Ludwig; Bruun, Tim-Henrik; Bogdahn, Ulrich.
Afiliación
  • Peters S; Department of Neurology, University Hospital Regensburg, 93053 Regensburg, Germany.
  • Wirkert E; Velvio GmbH, Am Biopark 11, 93053 Regensburg, Germany.
  • Kuespert S; Department of Neurology, University Hospital Regensburg, 93053 Regensburg, Germany.
  • Heydn R; Department of Neurology, University Hospital Regensburg, 93053 Regensburg, Germany.
  • Johannesen S; Department of Neurology, University Hospital Regensburg, 93053 Regensburg, Germany.
  • Friedrich A; Department of Neurology, University Hospital Regensburg, 93053 Regensburg, Germany.
  • Mailänder S; BG Trauma Center, Professor Küntscher Str. 8, 82418 Murnau am Staffelsee, Germany.
  • Korte S; Granzer Regulatory Consulting & Services, Kistlerhofstr. 172C, 81379 München, Germany.
  • Mecklenburg L; Granzer Regulatory Consulting & Services, Kistlerhofstr. 172C, 81379 München, Germany.
  • Aigner L; Labcorp Early Development Services GmbH, 48163 Münster, Germany.
  • Bruun TH; Labcorp Early Development Services GmbH, 48163 Münster, Germany.
  • Bogdahn U; Institute of Molecular Regenerative Medicine, Spinal Cord Injury and Tissue Regeneration Center Salzburg (SCI-TReCS), Paracelsus Medical University Salzburg, 5020 Salzburg, Austria.
Pharmaceutics ; 14(1)2022 Jan 15.
Article en En | MEDLINE | ID: mdl-35057094

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Idioma: En Revista: Pharmaceutics Año: 2022 Tipo del documento: Article País de afiliación: Alemania Pais de publicación: Suiza

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Idioma: En Revista: Pharmaceutics Año: 2022 Tipo del documento: Article País de afiliación: Alemania Pais de publicación: Suiza