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A double-blind, placebo-controlled, randomized trial of PXT3003 for the treatment of Charcot-Marie-Tooth type 1A.
Attarian, Shahram; Young, Peter; Brannagan, Thomas H; Adams, David; Van Damme, Philip; Thomas, Florian P; Casanovas, Carlos; Tard, Céline; Walter, Maggie C; Péréon, Yann; Walk, David; Stino, Amro; de Visser, Marianne; Verhamme, Camiel; Amato, Anthony; Carter, Gregory; Magy, Laurent; Statland, Jeffrey M; Felice, Kevin.
Afiliación
  • Attarian S; Reference Center for Neuromuscular Disorders and ALS, CHU La Timone, Marseille, France. Shahram.ATTARIAN@ap-hm.fr.
  • Young P; Department of Neurology, Medical Park Bad Feilnbach, Bad Feilnbach, Germany.
  • Brannagan TH; Columbia University Medical Center, The Neurological Institute, New York, USA.
  • Adams D; French Reference Center for Rare Peripheral Neuropathies, Service de Neurologie Adulte, APHP, CHU Bicêtre, Le Kremlin Bicêtre, France.
  • Van Damme P; Department of Neurology, University Hospitals Leuven, KU, Leuven, Belgium.
  • Thomas FP; Center for Brain & Disease Research, VIB, Leuven, Belgium.
  • Casanovas C; Department of Neurology, Hackensack University Medical Center, Hackensack, USA.
  • Tard C; Department of Neurology, Saint Louis University School of Medicine, St. Louis, USA.
  • Walter MC; Neuromuscular Unit, Neurology Department, Bellvitge University Hospital, Barcelona, Spain.
  • Péréon Y; Neurometabolic Diseases Group, Bellvitge Research Institute (IDIBELL) and CIBERER, Barcelona, Spain.
  • Walk D; U1171, Centre de référence des maladies neuromusculaires Nord Est Ile de France, Hôpital Salengro CHU de Lille, Lille, France.
  • Stino A; Department of Neurology, Friedrich-Baur-Institute, Ludwig-Maximilians-University of Munich, Munich, Germany.
  • de Visser M; Centre de Référence Maladies Neuromusculaires AOC, Filnemus, Euro-NMD, CHU Nantes, Hôtel-Dieu, Nantes, France.
  • Verhamme C; Clinical Neuroscience Research Unit, University of Minnesota, Minneapolis, USA.
  • Amato A; University of Michigan Health System, Ann Arbor, MI, USA.
  • Carter G; Department of Neurology, Amsterdam University Medical Centres, University of Amsterdam, Amsterdam Neuroscience, Amsterdam, The Netherlands.
  • Magy L; Department of Neurology, Amsterdam University Medical Centres, University of Amsterdam, Amsterdam Neuroscience, Amsterdam, The Netherlands.
  • Statland JM; Department of Neurology, Brigham and Women's Hospital, Boston, USA.
  • Felice K; St. Luke's Rehabilitation Institute, Physical Medicine and Rehabilitation, Spokane, USA.
Orphanet J Rare Dis ; 16(1): 433, 2021 10 16.
Article en En | MEDLINE | ID: mdl-34656144

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedad de Charcot-Marie-Tooth Tipo de estudio: Clinical_trials Límite: Humans Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2021 Tipo del documento: Article País de afiliación: Francia Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedad de Charcot-Marie-Tooth Tipo de estudio: Clinical_trials Límite: Humans Idioma: En Revista: Orphanet J Rare Dis Asunto de la revista: MEDICINA Año: 2021 Tipo del documento: Article País de afiliación: Francia Pais de publicación: Reino Unido