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The Effect of Immunomodulatory Treatments on Anti-Dystrophin Immune Response After AAV Gene Therapy in Dystrophin Deficient mdx Mice.
Li, Ning; Parkes, Joanna E; Spathis, Rita; Morales, Melissa; Mcdonald, John; Kendra, Ryan M; Ott, Emily M; Brown, Kristy J; Lawlor, Michael W; Nagaraju, Kanneboyina.
Afiliación
  • Li N; School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA.
  • Parkes JE; School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA.
  • Spathis R; School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA.
  • Morales M; School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA.
  • Mcdonald J; School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA.
  • Kendra RM; School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA.
  • Ott EM; Department of Pathology and Neuroscience Research Center, Medical College of Wisconsin, Milwaukee, WI, USA.
  • Brown KJ; Solid Biosciences Inc, Cambridge, MA, USA.
  • Lawlor MW; Department of Pathology and Neuroscience Research Center, Medical College of Wisconsin, Milwaukee, WI, USA.
  • Nagaraju K; School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA.
J Neuromuscul Dis ; 8(s2): S325-S340, 2021.
Article en En | MEDLINE | ID: mdl-34569971

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Terapia Genética / Distrofina / Dependovirus / Distrofia Muscular de Duchenne / Agentes Inmunomoduladores Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: J Neuromuscul Dis Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Países Bajos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Terapia Genética / Distrofina / Dependovirus / Distrofia Muscular de Duchenne / Agentes Inmunomoduladores Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: J Neuromuscul Dis Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Países Bajos