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A targeted antisense therapeutic approach for Hutchinson-Gilford progeria syndrome.
Erdos, Michael R; Cabral, Wayne A; Tavarez, Urraca L; Cao, Kan; Gvozdenovic-Jeremic, Jelena; Narisu, Narisu; Zerfas, Patricia M; Crumley, Stacy; Boku, Yoseph; Hanson, Gunnar; Mourich, Dan V; Kole, Ryszard; Eckhaus, Michael A; Gordon, Leslie B; Collins, Francis S.
Afiliación
  • Erdos MR; Molecular Genetics Section, Medical Genomics and Metabolic Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD, USA.
  • Cabral WA; Molecular Genetics Section, Medical Genomics and Metabolic Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD, USA.
  • Tavarez UL; Molecular Genetics Section, Medical Genomics and Metabolic Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD, USA.
  • Cao K; Department of Cell Biology and Molecular Genetics, University of Maryland, College Park, MD, USA.
  • Gvozdenovic-Jeremic J; Molecular Genetics Section, Medical Genomics and Metabolic Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD, USA.
  • Narisu N; Molecular Genetics Section, Medical Genomics and Metabolic Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD, USA.
  • Zerfas PM; Diagnostic and Research Services Branch, Division of Veterinary Resources, Office of Research Services, National Institutes of Health, Bethesda, MD, USA.
  • Crumley S; Sarepta Therapeutics, Inc., Cambridge, MA, USA.
  • Boku Y; Molecular Genetics Section, Medical Genomics and Metabolic Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD, USA.
  • Hanson G; Sarepta Therapeutics, Inc., Cambridge, MA, USA.
  • Mourich DV; Department of Veterinary Health Science, Oregon State University, Corvallis, OR, USA.
  • Kole R; Sarepta Therapeutics, Inc., Cambridge, MA, USA.
  • Eckhaus MA; Department of Pharmacology, University of North Carolina, Chapel Hill, NC, USA.
  • Gordon LB; Diagnostic and Research Services Branch, Division of Veterinary Resources, Office of Research Services, National Institutes of Health, Bethesda, MD, USA.
  • Collins FS; Department of Pediatrics, Hasbro Children's Hospital and Warren Alpert Medical School of Brown University, Providence, RI, USA.
Nat Med ; 27(3): 536-545, 2021 03.
Article en En | MEDLINE | ID: mdl-33707773

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Progeria / Oligonucleótidos Antisentido Límite: Animals / Humans Idioma: En Revista: Nat Med Asunto de la revista: BIOLOGIA MOLECULAR / MEDICINA Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Progeria / Oligonucleótidos Antisentido Límite: Animals / Humans Idioma: En Revista: Nat Med Asunto de la revista: BIOLOGIA MOLECULAR / MEDICINA Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Estados Unidos