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Attenuation of Heparan Sulfate Proteoglycan Binding Enhances In Vivo Transduction of Human Primary Hepatocytes with AAV2.
Cabanes-Creus, Marti; Westhaus, Adrian; Navarro, Renina Gale; Baltazar, Grober; Zhu, Erhua; Amaya, Anais K; Liao, Sophia H Y; Scott, Suzanne; Sallard, Erwan; Dilworth, Kimberley L; Rybicki, Arkadiusz; Drouyer, Matthieu; Hallwirth, Claus V; Bennett, Antonette; Santilli, Giorgia; Thrasher, Adrian J; Agbandje-McKenna, Mavis; Alexander, Ian E; Lisowski, Leszek.
Afiliación
  • Cabanes-Creus M; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.
  • Westhaus A; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.
  • Navarro RG; Great Ormond Street Institute of Child Health, University College London, London WC1N 1EH, UK.
  • Baltazar G; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.
  • Zhu E; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.
  • Amaya AK; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.
  • Liao SHY; Gene Therapy Research Unit, Children's Medical Research Institute & The Children's Hospital at Westmead, University of Sydney, Westmead, NSW 2145, Australia.
  • Scott S; Gene Therapy Research Unit, Children's Medical Research Institute & The Children's Hospital at Westmead, University of Sydney, Westmead, NSW 2145, Australia.
  • Sallard E; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.
  • Dilworth KL; Gene Therapy Research Unit, Children's Medical Research Institute & The Children's Hospital at Westmead, University of Sydney, Westmead, NSW 2145, Australia.
  • Rybicki A; Commonwealth Scientific and Industrial Research Organisation (CSIRO), North Ryde, NSW 2113, Australia.
  • Drouyer M; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.
  • Hallwirth CV; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.
  • Bennett A; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.
  • Santilli G; Translational Vectorology Research Unit, Children's Medical Research Institute, The University of Sydney, Westmead, NSW 2145, Australia.
  • Thrasher AJ; Gene Therapy Research Unit, Children's Medical Research Institute & The Children's Hospital at Westmead, University of Sydney, Westmead, NSW 2145, Australia.
  • Agbandje-McKenna M; Department of Biochemistry and Molecular Biology, Center for Structural Biology, University of Florida, Gainesville, FL 32610, USA.
  • Alexander IE; Great Ormond Street Institute of Child Health, University College London, London WC1N 1EH, UK.
  • Lisowski L; Great Ormond Street Institute of Child Health, University College London, London WC1N 1EH, UK.
Mol Ther Methods Clin Dev ; 17: 1139-1154, 2020 Jun 12.
Article en En | MEDLINE | ID: mdl-32490035

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Idioma: En Revista: Mol Ther Methods Clin Dev Año: 2020 Tipo del documento: Article País de afiliación: Australia Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Idioma: En Revista: Mol Ther Methods Clin Dev Año: 2020 Tipo del documento: Article País de afiliación: Australia Pais de publicación: Estados Unidos