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DCTN1-related Parkinson-plus disorder (Perry syndrome).
Richardson, Daniel; McEntagart, Meriel M; Isaacs, Jeremy D.
Afiliación
  • Richardson D; St George's, University of London, London, UK.
  • McEntagart MM; Medical Genetics Unit, St George's Hospital, London, UK.
  • Isaacs JD; Department of Neurology, St George's Hospital, London, UK jeremy.isaacs@nhs.net.
Pract Neurol ; 20(4): 317-319, 2020 Aug.
Article en En | MEDLINE | ID: mdl-32434902
Dynactin-1 (DCTN1)-related Parkinson-plus disorder (Perry syndrome) is an autosomal dominant neurodegenerative disorder characterised by levodopa-resistant parkinsonism, weight loss, mood change and central hypoventilation. Ventilatory insufficiency is the predominant cause of death. It has been previously described in 87 people from 20 families with a worldwide distribution. It is now recognised as a distinct TDP-43 proteinopathy caused by a pathological mutation in DCTN1. Its rarity and clinical overlap with other neurodegenerative diseases increase the risk of delayed or incorrect diagnosis. Ventilatory support can improve life expectancy but this depends upon its recognition; overall its prognosis remains poor. We report a patient with DCTN1-related Parkinson-plus disorder, in whom genetic confirmation came only after death.
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Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Trastornos Parkinsonianos / Disfunción Cognitiva / Complejo Dinactina / Hipoventilación Límite: Female / Humans / Middle aged Idioma: En Revista: Pract Neurol Año: 2020 Tipo del documento: Article Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Trastornos Parkinsonianos / Disfunción Cognitiva / Complejo Dinactina / Hipoventilación Límite: Female / Humans / Middle aged Idioma: En Revista: Pract Neurol Año: 2020 Tipo del documento: Article Pais de publicación: Reino Unido