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Optimizing lentiviral vector transduction of hematopoietic stem cells for gene therapy.
Jang, Yoonjeong; Kim, Yoon-Sang; Wielgosz, Matthew M; Ferrara, Francesca; Ma, Zhijun; Condori, Jose; Palmer, Lance E; Zhao, Xiwen; Kang, Guolian; Rawlings, David J; Zhou, Sheng; Ryu, Byoung Y.
Afiliación
  • Jang Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, 38105, USA.
  • Kim YS; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, 38105, USA.
  • Wielgosz MM; Mustang Bio, Worcester, MA, 01605, USA.
  • Ferrara F; Vector Development, St. Jude Children's Research Hospital, Memphis, TN, 38105, USA.
  • Ma Z; Vector Development, St. Jude Children's Research Hospital, Memphis, TN, 38105, USA.
  • Condori J; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, 38105, USA.
  • Palmer LE; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, 38105, USA.
  • Zhao X; Department of Computational Biology, St. Jude Children's Research Hospital, Memphis, TN, 38105, USA.
  • Kang G; Department of Biostatistics, St. Jude Children's Research Hospital, Memphis, TN, 38105, USA.
  • Rawlings DJ; Department of Biostatistics, St. Jude Children's Research Hospital, Memphis, TN, 38105, USA.
  • Zhou S; Center for Immunity and Immunotherapies, Seattle Children's Research Institute, and Department of Pediatrics, University of Washington School of Medicine, Seattle, WA, 98101, USA.
  • Ryu BY; Experimental Cellular Therapeutics Lab, St. Jude Children's Research Hospital, Memphis, TN, 38105, USA.
Gene Ther ; 27(12): 545-556, 2020 12.
Article en En | MEDLINE | ID: mdl-32341484

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Lentivirus / Trasplante de Células Madre Hematopoyéticas Tipo de estudio: Guideline Límite: Animals / Humans Idioma: En Revista: Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2020 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Lentivirus / Trasplante de Células Madre Hematopoyéticas Tipo de estudio: Guideline Límite: Animals / Humans Idioma: En Revista: Gene Ther Asunto de la revista: GENETICA MEDICA / TERAPEUTICA Año: 2020 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Reino Unido