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EBGene trial: patient preselection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa.
Gaucher, S; Lwin, S M; Titeux, M; Abdul-Wahab, A; Pironon, N; Izmiryan, A; Miskinyte, S; Ganier, C; Duchatelet, S; Mellerio, J E; Bourrat, E; McGrath, J A; Hovnanian, A.
Afiliación
  • Gaucher S; INSERM UMR 1163, Laboratory of Genetic Skin Diseases, Imagine Institute, Paris, France.
  • Lwin SM; University Paris Descartes-Sorbonne Paris Cité, Paris, France.
  • Titeux M; Service de Chirurgie Générale, Plastique et Ambulatoire, Assistance Publique-Hôpitaux de Paris, Hôpital Cochin, Paris, France.
  • Abdul-Wahab A; St John's Institute of Dermatology, King's College London, London, U.K.
  • Pironon N; INSERM UMR 1163, Laboratory of Genetic Skin Diseases, Imagine Institute, Paris, France.
  • Izmiryan A; St John's Institute of Dermatology, King's College London, London, U.K.
  • Miskinyte S; INSERM UMR 1163, Laboratory of Genetic Skin Diseases, Imagine Institute, Paris, France.
  • Ganier C; University Paris Descartes-Sorbonne Paris Cité, Paris, France.
  • Duchatelet S; INSERM UMR 1163, Laboratory of Genetic Skin Diseases, Imagine Institute, Paris, France.
  • Mellerio JE; University Paris Descartes-Sorbonne Paris Cité, Paris, France.
  • Bourrat E; INSERM UMR 1163, Laboratory of Genetic Skin Diseases, Imagine Institute, Paris, France.
  • McGrath JA; INSERM UMR 1163, Laboratory of Genetic Skin Diseases, Imagine Institute, Paris, France.
  • Hovnanian A; INSERM UMR 1163, Laboratory of Genetic Skin Diseases, Imagine Institute, Paris, France.
Br J Dermatol ; 182(3): 794-797, 2020 03.
Article en En | MEDLINE | ID: mdl-31557321

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Epidermólisis Ampollosa Distrófica / Epidermólisis Ampollosa Límite: Humans Idioma: En Revista: Br J Dermatol Año: 2020 Tipo del documento: Article País de afiliación: Francia Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Epidermólisis Ampollosa Distrófica / Epidermólisis Ampollosa Límite: Humans Idioma: En Revista: Br J Dermatol Año: 2020 Tipo del documento: Article País de afiliación: Francia Pais de publicación: Reino Unido