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Specific inhibition of myostatin activation is beneficial in mouse models of SMA therapy.
Long, Kimberly K; O'Shea, Karen M; Khairallah, Ramzi J; Howell, Kelly; Paushkin, Sergey; Chen, Karen S; Cote, Shaun M; Webster, Micah T; Stains, Joseph P; Treece, Erin; Buckler, Alan; Donovan, Adriana.
Afiliación
  • Long KK; Scholar Rock Inc., 620 Memorial Drive, Cambridge, MA.
  • O'Shea KM; Myologica, 10811 Dewey Way East, New Market, MD.
  • Khairallah RJ; Myologica, 10811 Dewey Way East, New Market, MD.
  • Howell K; SMA Foundation, 888 7th Avenue #400, New York, NY.
  • Paushkin S; SMA Foundation, 888 7th Avenue #400, New York, NY.
  • Chen KS; SMA Foundation, 888 7th Avenue #400, New York, NY.
  • Cote SM; Scholar Rock Inc., 620 Memorial Drive, Cambridge, MA.
  • Webster MT; Scholar Rock Inc., 620 Memorial Drive, Cambridge, MA.
  • Stains JP; Department of Orthopedics, University of Maryland School of Medicine, Baltimore, MD, USA.
  • Treece E; Scholar Rock Inc., 620 Memorial Drive, Cambridge, MA.
  • Buckler A; Scholar Rock Inc., 620 Memorial Drive, Cambridge, MA.
  • Donovan A; Scholar Rock Inc., 620 Memorial Drive, Cambridge, MA.
Hum Mol Genet ; 28(7): 1076-1089, 2019 04 01.
Article en En | MEDLINE | ID: mdl-30481286

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Atrofia Muscular Espinal / Miostatina Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Hum Mol Genet Asunto de la revista: BIOLOGIA MOLECULAR / GENETICA MEDICA Año: 2019 Tipo del documento: Article País de afiliación: Marruecos Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Atrofia Muscular Espinal / Miostatina Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Hum Mol Genet Asunto de la revista: BIOLOGIA MOLECULAR / GENETICA MEDICA Año: 2019 Tipo del documento: Article País de afiliación: Marruecos Pais de publicación: Reino Unido