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Robust erythroid differentiation system for rhesus hematopoietic progenitor cells allowing preclinical screening of genetic treatment strategies for the hemoglobinopathies.
Demirci, Selami; Bhardwaj, Saurabh K; Uchida, Naoya; Haro-Mora, Juan J; Ryu, Byoung; Blobel, Gerd A; Tisdale, John F.
Afiliación
  • Demirci S; Sickle Cell Branch, National Heart Lung and Blood Institutes/National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health, Bethesda, MD, USA.
  • Bhardwaj SK; Department of Pediatrics, Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, PA, USA.
  • Uchida N; Sickle Cell Branch, National Heart Lung and Blood Institutes/National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health, Bethesda, MD, USA. Electronic address: uchidan@nhlbi.nih.gov.
  • Haro-Mora JJ; Sickle Cell Branch, National Heart Lung and Blood Institutes/National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health, Bethesda, MD, USA.
  • Ryu B; Experimental Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA.
  • Blobel GA; Department of Pediatrics, Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, PA, USA.
  • Tisdale JF; Sickle Cell Branch, National Heart Lung and Blood Institutes/National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health, Bethesda, MD, USA.
Cytotherapy ; 20(10): 1278-1287, 2018 10.
Article en En | MEDLINE | ID: mdl-30249524

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Células Madre Hematopoyéticas / Terapia Genética / Técnicas de Cultivo de Célula / Gamma-Globinas Tipo de estudio: Diagnostic_studies / Guideline / Prognostic_studies / Screening_studies Límite: Animals / Humans Idioma: En Revista: Cytotherapy Asunto de la revista: TERAPEUTICA Año: 2018 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Células Madre Hematopoyéticas / Terapia Genética / Técnicas de Cultivo de Célula / Gamma-Globinas Tipo de estudio: Diagnostic_studies / Guideline / Prognostic_studies / Screening_studies Límite: Animals / Humans Idioma: En Revista: Cytotherapy Asunto de la revista: TERAPEUTICA Año: 2018 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Reino Unido