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Combination potentiator ('co-potentiator') therapy for CF caused by CFTR mutants, including N1303K, that are poorly responsive to single potentiators.
Phuan, Puay-Wah; Son, Jung-Ho; Tan, Joseph-Anthony; Li, Clarabella; Musante, Ilaria; Zlock, Lorna; Nielson, Dennis W; Finkbeiner, Walter E; Kurth, Mark J; Galietta, Luis J; Haggie, Peter M; Verkman, Alan S.
Afiliación
  • Phuan PW; Department of Medicine, University of California, San Francisco, CA 94143-0521, USA; Department of Physiology, University of California, San Francisco, CA 94143-0521, USA. Electronic address: Puay-wah.Phuan@ucsf.edu.
  • Son JH; Department of Chemistry, University of California, Davis, CA 95616-5270, USA.
  • Tan JA; Department of Medicine, University of California, San Francisco, CA 94143-0521, USA; Department of Physiology, University of California, San Francisco, CA 94143-0521, USA.
  • Li C; Department of Chemistry, University of California, Davis, CA 95616-5270, USA.
  • Musante I; Telethon Institute for Genetics and Medicine (TIGEM), Pozzuoli, Italy.
  • Zlock L; Department of Pathology University of California, San Francisco, CA 94143-0521, USA.
  • Nielson DW; Department of Pediatrics, University of California, San Francisco, CA 94143-0521, USA.
  • Finkbeiner WE; Department of Pathology University of California, San Francisco, CA 94143-0521, USA.
  • Kurth MJ; Department of Chemistry, University of California, Davis, CA 95616-5270, USA.
  • Galietta LJ; Telethon Institute for Genetics and Medicine (TIGEM), Pozzuoli, Italy.
  • Haggie PM; Department of Medicine, University of California, San Francisco, CA 94143-0521, USA; Department of Physiology, University of California, San Francisco, CA 94143-0521, USA.
  • Verkman AS; Department of Medicine, University of California, San Francisco, CA 94143-0521, USA; Department of Physiology, University of California, San Francisco, CA 94143-0521, USA.
J Cyst Fibros ; 17(5): 595-606, 2018 09.
Article en En | MEDLINE | ID: mdl-29903467

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Sulfonamidas / Quinolonas / Regulador de Conductancia de Transmembrana de Fibrosis Quística / Fibrosis Quística / Aminofenoles Límite: Animals / Humans Idioma: En Revista: J Cyst Fibros Año: 2018 Tipo del documento: Article Pais de publicación: Países Bajos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Sulfonamidas / Quinolonas / Regulador de Conductancia de Transmembrana de Fibrosis Quística / Fibrosis Quística / Aminofenoles Límite: Animals / Humans Idioma: En Revista: J Cyst Fibros Año: 2018 Tipo del documento: Article Pais de publicación: Países Bajos