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Nusinersen for SMA: expanded access programme.
Farrar, Michelle A; Teoh, Hooi Ling; Carey, Kate A; Cairns, Anita; Forbes, Robin; Herbert, Karen; Holland, Sandra; Jones, Kristi J; Menezes, Manoj P; Morrison, Margot; Munro, Kate; Villano, Daniella; Webster, Richard; Woodcock, Ian R; Yiu, Eppie M; Sampaio, Hugo; Ryan, Monique M.
Afiliación
  • Farrar MA; Department of Neurology, Sydney Children's Hospitals Network, Sydney, Australia.
  • Teoh HL; School of Women's and Children's Health, UNSW Medicine, The University of New South Wales, Sydney, Australia.
  • Carey KA; Department of Neurology, Sydney Children's Hospitals Network, Sydney, Australia.
  • Cairns A; School of Women's and Children's Health, UNSW Medicine, The University of New South Wales, Sydney, Australia.
  • Forbes R; Department of Neurology, Sydney Children's Hospitals Network, Sydney, Australia.
  • Herbert K; School of Women's and Children's Health, UNSW Medicine, The University of New South Wales, Sydney, Australia.
  • Holland S; Department of Neurology, Lady Cilento Children's Hospital, Brisbane, Australia.
  • Jones KJ; Department of Neurology, The Royal Children's Hospital, Melbourne, Australia.
  • Menezes MP; Murdoch Children's Research Institute, Melbourne, Australia.
  • Morrison M; Department of Physiotherapy, Sydney Children's Hospitals Network, Sydney, Australia.
  • Munro K; Department of Neurology, Sydney Children's Hospitals Network, Sydney, Australia.
  • Villano D; Department of Neurology, Sydney Children's Hospitals Network, Sydney, Australia.
  • Webster R; Discipline of Paediatrics and Child Health, The Children's Hospital at Westmead Clinical School, The University of Sydney, Sydney, Australia.
  • Woodcock IR; Department of Neurology, Sydney Children's Hospitals Network, Sydney, Australia.
  • Yiu EM; Discipline of Paediatrics and Child Health, The Children's Hospital at Westmead Clinical School, The University of Sydney, Sydney, Australia.
  • Sampaio H; Department of Neurology, Sydney Children's Hospitals Network, Sydney, Australia.
  • Ryan MM; Department of Neurology, Lady Cilento Children's Hospital, Brisbane, Australia.
J Neurol Neurosurg Psychiatry ; 89(9): 937-942, 2018 09.
Article en En | MEDLINE | ID: mdl-29549190

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Oligonucleótidos / Atrofias Musculares Espinales de la Infancia / Accesibilidad a los Servicios de Salud Tipo de estudio: Clinical_trials / Observational_studies / Prognostic_studies / Screening_studies Aspecto: Determinantes_sociais_saude / Ethics Límite: Child, preschool / Female / Humans / Infant / Male País/Región como asunto: Oceania Idioma: En Revista: J Neurol Neurosurg Psychiatry Año: 2018 Tipo del documento: Article País de afiliación: Australia Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Oligonucleótidos / Atrofias Musculares Espinales de la Infancia / Accesibilidad a los Servicios de Salud Tipo de estudio: Clinical_trials / Observational_studies / Prognostic_studies / Screening_studies Aspecto: Determinantes_sociais_saude / Ethics Límite: Child, preschool / Female / Humans / Infant / Male País/Región como asunto: Oceania Idioma: En Revista: J Neurol Neurosurg Psychiatry Año: 2018 Tipo del documento: Article País de afiliación: Australia Pais de publicación: Reino Unido