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High Sustained Antibody Titers in Patients with Classic Infantile Pompe Disease Following Immunomodulation at Start of Enzyme Replacement Therapy.
Poelman, Esther; Hoogeveen-Westerveld, Marianne; Kroos-de Haan, Marian A; van den Hout, Johanna M P; Bronsema, Kees J; van de Merbel, Nico C; van der Ploeg, Ans T; Pijnappel, W W M Pim.
Afiliación
  • Poelman E; Center for Lysosomal and Metabolic Diseases, Erasmus Medical Center, Rotterdam, The Netherlands; Department of Pediatrics, Division of Metabolic Diseases and Genetics, Erasmus MC University Medical Center, Rotterdam, The Netherlands.
  • Hoogeveen-Westerveld M; Center for Lysosomal and Metabolic Diseases, Erasmus Medical Center, Rotterdam, The Netherlands; Department of Clinical Genetics, Erasmus Medical Center, Rotterdam, The Netherlands.
  • Kroos-de Haan MA; Center for Lysosomal and Metabolic Diseases, Erasmus Medical Center, Rotterdam, The Netherlands; Department of Clinical Genetics, Erasmus Medical Center, Rotterdam, The Netherlands.
  • van den Hout JMP; Center for Lysosomal and Metabolic Diseases, Erasmus Medical Center, Rotterdam, The Netherlands; Department of Pediatrics, Division of Metabolic Diseases and Genetics, Erasmus MC University Medical Center, Rotterdam, The Netherlands.
  • Bronsema KJ; Bioanalytical Laboratory, PRA Health Sciences, Early Development Services, Assen, The Netherlands; Analytical Biochemistry, Department of Pharmacy, University of Groningen, Groningen, The Netherlands.
  • van de Merbel NC; Bioanalytical Laboratory, PRA Health Sciences, Early Development Services, Assen, The Netherlands; Analytical Biochemistry, Department of Pharmacy, University of Groningen, Groningen, The Netherlands.
  • van der Ploeg AT; Center for Lysosomal and Metabolic Diseases, Erasmus Medical Center, Rotterdam, The Netherlands; Department of Pediatrics, Division of Metabolic Diseases and Genetics, Erasmus MC University Medical Center, Rotterdam, The Netherlands.
  • Pijnappel WWMP; Center for Lysosomal and Metabolic Diseases, Erasmus Medical Center, Rotterdam, The Netherlands; Department of Pediatrics, Division of Metabolic Diseases and Genetics, Erasmus MC University Medical Center, Rotterdam, The Netherlands; Department of Clinical Genetics, Erasmus Medical Center, Rotterdam
J Pediatr ; 195: 236-243.e3, 2018 04.
Article en En | MEDLINE | ID: mdl-29428273

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedad del Almacenamiento de Glucógeno Tipo II / Alfa-Glucosidasas / Inmunomodulación / Terapia de Reemplazo Enzimático / Anticuerpos Tipo de estudio: Observational_studies / Prognostic_studies / Risk_factors_studies Límite: Child, preschool / Female / Humans / Infant / Male Idioma: En Revista: J Pediatr Año: 2018 Tipo del documento: Article País de afiliación: Países Bajos Pais de publicación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Enfermedad del Almacenamiento de Glucógeno Tipo II / Alfa-Glucosidasas / Inmunomodulación / Terapia de Reemplazo Enzimático / Anticuerpos Tipo de estudio: Observational_studies / Prognostic_studies / Risk_factors_studies Límite: Child, preschool / Female / Humans / Infant / Male Idioma: En Revista: J Pediatr Año: 2018 Tipo del documento: Article País de afiliación: Países Bajos Pais de publicación: Estados Unidos