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Quality of Life and Participation in the Daily Life (Activities) of Adults with Pompe Disease Receiving Enzyme Replacement Therapy: 10 Years of International Follow-Up.
Güngör, D; Kruijshaar, M E; Plug, I; Rizopoulos, D; Kanters, T A; Wens, S C A; Reuser, A J J; van Doorn, P A; van der Ploeg, A T.
Afiliación
  • Güngör D; Center for Lysosomal and Metabolic diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands.
  • Kruijshaar ME; Center for Lysosomal and Metabolic diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands.
  • Plug I; Center for Lysosomal and Metabolic diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands.
  • Rizopoulos D; Department of Biostatistics, Erasmus MC University Medical Center, Rotterdam, Netherlands.
  • Kanters TA; Department of Health Policy and Management, Institute for Medical Technology Assessment, Erasmus University Rotterdam, Rotterdam, Netherlands.
  • Wens SC; Department of Neurology, Erasmus MC University Medical Center, Rotterdam, Netherlands.
  • Reuser AJ; Department of Clinical Genetics, Erasmus MC University Medical Center, Rotterdam, The Netherlands.
  • van Doorn PA; Department of Neurology, Erasmus MC University Medical Center, Rotterdam, Netherlands.
  • van der Ploeg AT; Center for Lysosomal and Metabolic diseases, Erasmus MC University Medical Center, Rotterdam, Netherlands.
J Neuromuscul Dis ; 2(s1): S63, 2015.
Article en En | MEDLINE | ID: mdl-27858652
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Colección: 01-internacional Base de datos: MEDLINE Aspecto: Patient_preference Idioma: En Revista: J Neuromuscul Dis Año: 2015 Tipo del documento: Article País de afiliación: Países Bajos Pais de publicación: Países Bajos
Buscar en Google
Colección: 01-internacional Base de datos: MEDLINE Aspecto: Patient_preference Idioma: En Revista: J Neuromuscul Dis Año: 2015 Tipo del documento: Article País de afiliación: Países Bajos Pais de publicación: Países Bajos