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Everolimus for subependymal giant cell astrocytoma in patients with tuberous sclerosis complex: 2-year open-label extension of the randomised EXIST-1 study.
Franz, David Neal; Belousova, Elena; Sparagana, Steven; Bebin, E Martina; Frost, Michael; Kuperman, Rachel; Witt, Olaf; Kohrman, Michael H; Flamini, J Robert; Wu, Joyce Y; Curatolo, Paolo; de Vries, Petrus J; Berkowitz, Noah; Anak, Oezlem; Niolat, Julie; Jozwiak, Sergiusz.
Afiliación
  • Franz DN; Department of Neurology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA. Electronic address: david.franz@cchmc.org.
  • Belousova E; Moscow Research Institute of Pediatrics and Pediatric Surgery, Moscow, Russia.
  • Sparagana S; Department of Neurology, Texas Scottish Rite Hospital for Children, Dallas, TX, USA.
  • Bebin EM; Department of Neurology, University of Alabama School of Medicine, Birmingham, AL, USA.
  • Frost M; Department of Neurology, Minnesota Epilepsy Group, St Paul, MN, USA.
  • Kuperman R; Department of Neurology, Children's Hospital and Research Center, Oakland, CA, USA.
  • Witt O; Department of Oncology, University of Heidelberg Medical Center and German Cancer Research Center, Heidelberg, Germany.
  • Kohrman MH; Department of Neurology, University of Chicago, Chicago, IL, USA.
  • Flamini JR; Department of Neurology, Children's Healthcare of Atlanta, Atlanta, GA, USA.
  • Wu JY; Department of Neurology, Mattel Children's Hospital, University of California, Los Angeles, Los Angeles, CA, USA.
  • Curatolo P; Department of Neurology, University of Rome Tor Vergata, Rome, Italy.
  • de Vries PJ; Department of Psychiatry and Mental Health, Division of Child and Adolescent Psychiatry, University of Cape Town, South Africa.
  • Berkowitz N; Department of Oncology, Novartis Pharmaceuticals Corporation, East Hanover, NJ, USA.
  • Anak O; Department of Oncology, Novartis Pharmaceuticals Corporation, East Hanover, NJ, USA.
  • Niolat J; Novartis Pharmaceuticals SAS, Rueil-Malmaison, France.
  • Jozwiak S; Department of Neurology, Children's Memorial Health Institute, Al Dzieci Polskich 20, Warsaw, Poland.
Lancet Oncol ; 15(13): 1513-1520, 2014 Dec.
Article en En | MEDLINE | ID: mdl-25456370

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Astrocitoma / Esclerosis Tuberosa / Sirolimus / Inmunosupresores Tipo de estudio: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Límite: Adult / Female / Humans / Male Idioma: En Revista: Lancet Oncol Asunto de la revista: NEOPLASIAS Año: 2014 Tipo del documento: Article Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Astrocitoma / Esclerosis Tuberosa / Sirolimus / Inmunosupresores Tipo de estudio: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Límite: Adult / Female / Humans / Male Idioma: En Revista: Lancet Oncol Asunto de la revista: NEOPLASIAS Año: 2014 Tipo del documento: Article Pais de publicación: Reino Unido